Donate to get LBSL research across the finish line!

Two gene therapies have been identified by the team at Kennedy Krieger and two other hospitals are looking for new drugs that can be repurposed. This has been a long road and it's not over yet. We still need to test for toxicity and get FDA approval for human trials. We would be no where without our supporters - our friends, family and affected patients around the world. Let's keep the momentum - keep fighting. Cures are close. We love you all.